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Registry: Identity Supplement: 0 FontDescriptor: FontName: SPFNQJ+Symbol Flags: Serif, Symbolic FontBBox: -180, -293, 1090, 1010 FontFile3: true XMP: Adobe PDF Library 8.0 False 2011-10-14T20:21:35-07:00 Adobe InDesign CS3 (5.0) Molecular Therapy (2011). doi:10.1038/mt.2011.220 2011-10-14T21:08:51-07:00 2011-10-14T21:08:51-07:00 doi:10.1038/mt.2011.220/nature06264 uuid:27bf4dc2-daa2-46a0-9944-4aeea86cb8d0 uuid:c684b10c-f8b3-4372-83b9-cf9ad6cbd61c True © 2011 Nature Publishing Group 10.1038/mt.2011.220 1525-0024 1525-0016 Molecular Therapy permissions@nature.com http://dx.doi.org/10.1038/mt.2011.220/nature06264 2009-11-13 application/pdf doi:10.1038/mt.2011.220 Molecular Therapy (2011). doi:10.1038/mt.2011.220 Nature Publishing Group © 2009 Nature Publishing Group Liver Production of Sulfamidase Reverses Peripheral and Ameliorates CNS Pathology in Mucopolysaccharidosis IIIA Mice Albert Ruzo Miquel Garcia Albert Ribera Pilar Villacampa Virginia Haurigot Sara Marcó Eduard Ayuso Xavier M Anguela Carles Roca Judith Agudo David Ramos Jesús Ruberte Fatima Bosch Pages: Page: Sequence: 1 Page: Sequence: 2 Page: Sequence: 3 Page: Sequence: 4 Page: Sequence: 5 Page: Sequence: 6 Page: Sequence: 7 Page: Sequence: 8 Page: Sequence: 9 Page: Sequence: 10 Page: Sequence: 11 Page: Sequence: 12 Page: Sequence: 13 Checksum: e3a485a2 Type: CRC32 Checksum: 77f31fb1175e854df3f2459e3889799e Type: MD5 Checksum: 76952be0341d34da1d9f583321fccb1edc688676 Type: SHA-1 Checksum: 1d5d36a542091289b3759b7608516ce4417b7beabe6a65444688323e2443afd4 Type: SHA-256