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phase 2 study of ACE-083, a muscle-promoting agent, in facioscapulohumeral muscular dystrophy Destination: atl_MUS_27558_ Children: Item: Title: 1 INTRODUCTION Destination: HeadingMUS_27558mus27558-sec-0005 Item: Title: 2 2 METHODS Destination: HeadingMUS_27558mus27558-sec-0006 Children: Item: Title: 2.1 Study design Destination: HeadingMUS_27558mus27558-sec-0007 Item: Title: 2.2 Standard protocol approvals, registrations, and patient consent Destination: HeadingMUS_27558mus27558-sec-0008 Children: Item: Title: 2.2.1 Participants Destination: HeadingMUS_27558mus27558-sec-0009 Item: Title: 2.3 Treatment Destination: HeadingMUS_27558mus27558-sec-0010 Item: Title: 2.4 Outcome measures Destination: HeadingMUS_27558mus27558-sec-0011 Children: Item: Title: 2.4.1 MRI measures Destination: HeadingMUS_27558mus27558-sec-0012 Item: Title: 2.4.2 Motor function, PRO, and strength Destination: HeadingMUS_27558mus27558-sec-0013 Item: Title: 2.4.3 Safety Destination: HeadingMUS_27558mus27558-sec-0014 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