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Articles, 2 records found
Articles 2 records found  
1.
8 p, 867.3 KB Prenatal dexamethasone treatment for classic 21-hydroxylase deficiency in Europe / Nowotny, Hanna (Universität München) ; Neumann, Uta (Charité - Universitätsmedizin Berlin) ; Tardy-Guidollet, Véronique (Université Lyon I) ; Ahmed, S. Faisal (University of Glasgow) ; Baronio, Federico (Paediatric Endocrinology Unit) ; Battelino, Tadej (Department of Endocrinology) ; Bertherat, Jérôme (Hôpitaux Universitaires Paris-Centre) ; Blankenstein, Oliver (Charité - Universitätsmedizin Berlin) ; Bonomi, Marco (University of Milan) ; Bouvattier, Claire (Hôpital de Bicêtre) ; Brac de la Perrière, Aude (Fédération d'Endocrinologie) ; Brucker, Sara (Department of Women's Health) ; Cappa, Marco (Endocrinology Unit) ; Chanson, Philippe (Assistance Publique-Hôpitaux de Paris) ; Claahsen-van der Grinten, Hedi L. (Amalia Children's Hospital) ; Colao, Annamaria (Universita' Federico II di Napoli) ; Cools, Martine (Universitair Ziekenhuis Gent) ; Davies, Justin H. (Universitair Ziekenhuis Gent) ; Dörr, Helmut-Günther (Universitätsklinikum Erlangen) ; Fenske, Wiebke K. (University Hospital Bonn (Bonn, Alemanya)) ; Ghigo, Ezio (University of Turin) ; Giordano, Roberta (University of Turin) ; Gravholt, Claus H. (Aarhus University Hospital (Aarhus, Dinamarca)) ; Huebner, Angela (Universitätsklinikum Dresden) ; Husebye, Eystein Sverre (Haukeland University Hospital (Bergen, Noruega)) ; Igbokwe, Rebecca (Birmingham Women's Hospital) ; Juul, Anders (Copenhagen University Hospital) ; Kiefer, Florian W. (University of Vienna) ; Léger, Juliane (AP-HP Paris Nord Université de Paris) ; Menassa, Rita (Université Lyon I) ; Meyer, Gesine (Goethe University Frankfurt) ; Neocleous, Vassos (Cyprus School of Molecular Medicine) ; Phylactou, Leonidas A. (Cyprus School of Molecular Medicine) ; Rohayem, Julia (Centre of Reproductive Medicine and Andrology) ; Russo, Gianni (Scientific Institute San Raffaele) ; Scaroni, Carla (Università di Padova) ; Touraine, Philippe (Sorbonne Université) ; Unger, Nicole (University Hospital Essen (Alemanya)) ; Vojtková, Jarmila (Comenius University in Bratislava) ; Yeste Fernández, Diego (Hospital Universitari Vall d'Hebron) ; Lajic, Svetlana (Karolinska University Hospital and Karolinska Institutet (Suècia)) ; Reisch, Nicole (Medizinische Klinik und Poliklinik IV) ; Universitat Autònoma de Barcelona
To assess the current medical practice in Europe regarding prenatal dexamethasone (Pdex) treatment of congenital adrenal hyperplasia (CAH) due to 21-hydroxylase deficiency. A questionnaire was designed and distributed, including 17 questions collecting quantitative and qualitative data. [...]
2022 - 10.1530/EJE-21-0554
European journal of endocrinology, Vol. 186 (march 2022) , p. K17-K24  
2.
12 p, 755.8 KB A randomised, open-label, parallel group phase 2 study of antisense oligonucleotide therapy in acromegaly / Trainer, Peter J. (Department of Endocrinology) ; Newell-Price, John D. C. (Royal Hallamshire Hospital) ; Ayuk, John (Medicine Endocrinology) ; Aylwin, Simon J. B. (King's College Hospital NHS Foundation Trust) ; Rees, Aled (Neuroscience and Mental Health Research Institute) ; Drake, William (Department of Endocrinology) ; Chanson, Philippe (Inserm 1185) ; Brue, Thierry (APHM) ; Webb, S. M 1952- (Institut d'Investigació Biomèdica Sant Pau) ; Fajardo, Carmen (Servicio de Endocrinología) ; Aller, Javier (Endocrinology Department) ; McCormack, Ann I (Garvan Institute of Medical Research and St Vincent's Hospital) ; Torpy, David J. (Royal Adelaide Hospital) ; Tachas, George (Antisense Therapeutics Limited) ; Atley, Lynne (Antisense Therapeutics Limited) ; Ryder, David (Manchester Academic Health Science Centre (MAHSC) Clinical Trials Unit) ; Bidlingmaier, Martin (Endocrine Laboratory) ; Universitat Autònoma de Barcelona
ATL1103 is a second-generation antisense oligomer targeting the human growth hormone (GH) receptor. This phase 2 randomised, open-label, parallel-group study assessed the potential of ATL1103 as a treatment for acromegaly. [...]
2018 - 10.1530/EJE-18-0138
European journal of endocrinology, Vol. 179 (may 2018) , p. 97-108  

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3 Chanson, P.
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