1.
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19 p, 3.2 MB |
Hematopoietic cell transplantation in severe combined immunodeficiency : The SCETIDE 2006-2014 European cohort
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Lankester, Arjan C. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Neven, Benedicte (Institut Imagine. INSERM UMR1163. Laboratory of Immunogenetics of Pediatric Autoimmune Diseases) ;
Mahlaoui, Nizar (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
von Asmuth, Erik G.J. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Courteille, Virginie (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Alligon, Mikael (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Albert, Michael H. (Dr von Haunersches University Children's Hospital) ;
Badell Serra, Isabel (Institut d'Investigació Biomèdica Sant Pau) ;
Bader, Peter (Department for Children and Adolescents Medicine. Division for Stem Cell Transplantation and Immunology. University Hospital Frankfurt) ;
Balashov, Dmitry (Department for Hematopoietic Stem Cell Transplantation. Dmitriy Rogachev National Center for Pediatric Hematology. Oncology and Immunology) ;
Beier, Rita (Klinik für Pädiatrische Hämatologie und Onkologie. Hannover Medical School) ;
Bertrand, Yves (Institut d'Hématologie et d'Oncologie Pédiatrique. Hospices Civils de Lyon and Université Claude Bernard Lyon 1) ;
Blanche, Stephane (Unité d'Immuno-hematologie et Rhumatologie Pédiatrique. Hôpital Universitaire Necker-Enfants Malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Bordon, Victoria (Department of Pediatric Hemato-oncology and Stem Cell Transplant. Ghent University Hospital) ;
Bredius, Robert G. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Cant, Andrew (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital) ;
Cavazzana, Marina (Laboratory of Genomic Dynamics in the Immune System. Institut Imagine. INSERM UMR1163) ;
Díaz de Heredia, Cristina (Vall d'Hebron Institut d'Oncologia) ;
Dogu, Figen (Department of PIA and the BMT Unit. Ankara University) ;
Ehlert, Karoline (Department of Pediatric Hematology and Oncology. University of Greifswald) ;
Entz-Werle, Natacha (Pediatric Onco-hematology Department-Pediatrics III. University Hospital of Strasbourg) ;
Fasth, Anders (Department of Pediatrics. Institute of Clinical Sciences. University of Gothenburg) ;
Ferrua, Francesca (Pediatric Immunohematology and Bone Marrow Transplantation Unit and the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget). IRCCS San Raffaele Scientific Institute) ;
Ferster, Alina (Department of Hemato-oncology. Hôpital Universitaire des Enfants Reine Fabiola) ;
Formankova, Renata (Department of Pediatric Hematology and Oncology. Teaching Hospital Motol. 2nd Medical School. Charles University Motol) ;
Friedrich, Wilhelm (Department of Pediatrics. University Medical Center Ulm) ;
Gonzalez-Vicent, Marta (Hospital del Niño Jesús. Hematopoietic Stem Cell Transplantation and Cellular Therapy Unit) ;
Gozdzik, Jolanta (Department of Clinical Immunology and Transplantation. Jagiellonian University Medical College) ;
Güngör, Tayfun (Department of Hematology. Oncology. Immunology. Gene Therapy and Stem Cell Transplantation. and Children's Research Center (CRC). University Children's Hospital) ;
Hoenig, Manfred (Department of Pediatrics. University Medical Center Ulm) ;
Ikinciogullari, Aydan (Department of PIA and the BMT Unit. Ankara University) ;
Kalwak, Krzysztof (Department of Pediatric Hematology. Oncology. and BMT. Wroclaw Medical University) ;
Kansoy, Savas (Department of Pediatric Hematology and Oncology. Ege University Hospital) ;
Kupesiz, Alphan (Department of Pediatrics. Hematology. and Oncology. Akdeniz University School of Medicine) ;
Lanfranchi, Arnalda (Diagnostic Department. Stem Cell Laboratory. Section of Hematology and Blood Coagulation. Clinical Chemistry Laboratory. ASST Spedali Civili) ;
Lindemans, Caroline A. (Department of Pediatrics. University Medical Center Utrecht. University of Utrecht) ;
Meisel, Roland (Department of Pediatric Oncology. Hematology. and Clinical Immunology. Medical Faculty. Division of Pediatric Stem Cell Therapy. Heinrich-Heine-University) ;
Michel, Gerard (Service d'Hématologie Immunologie Oncologie Pédiatrique. CHU La Timone) ;
Miranda, Nuno A. A. (BMT Unit. Instituto Português de Oncologia de Lisboa) ;
Moraleda, Jose (Hospital Virgen de la Arrixaca. Instituto Murciano de Investigación Biosanitaria) ;
Moshous, Despina (Laboratory of Genomic Dynamics in the Immune System. Institut Imagine. INSERM UMR1163) ;
Pichler, Herbert (Department of Stem Cell Transplantation. Children's Cancer Institute. St Anna Hospital) ;
Rao, Kanchan (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Sedlacek, Petr (Department of Pediatric Hematology and Oncology. Teaching Hospital Motol. 2nd Medical School. Charles University Motol) ;
Slatter, Mary (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital) ;
Soncini, Elena (Pediatric Oncohaematology and BMT Unit. Children's Hospital Brescia) ;
Speckmann, Carsten (Department of Pediatric Hematology and Oncology. Center for Pediatrics and Adolescent Medicine. Institute for Immunodeficiency. Center for Chronic Immunodeficiency (CCI). Faculty of Medicine. Medical Center. University of Freiburg) ;
Sundin, Mikael (Section of Pediatric Hematology. Immunology. and HCT. Astrid Lindgren Children's Hospital. Karolinska University Hospital. and Division of Pediatrics. CLINTEC. Karolinska Institutet) ;
Toren, Amos (Paediatric Hemato-oncology and BMT. Sheba Medical Center) ;
Vettenranta, Kim (University of Helsinki and Children's Hospital. University of Helsinki) ;
Worth, Austen (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Yeşilipek, Mehmet A. (Pediatric Hematology. Oncology. and Pediatric Stem Cell Transplantation Unit. Medicalpark Antalya & Göztepe Hospitals) ;
Zecca, Marco (Pediatric Hematology/Oncology. Fondazione IRCCS Policlinico San Matteo) ;
Porta, Fulvio (Pediatric Oncohaematology and BMT Unit. Children's Hospital Brescia) ;
Schulz, Ansgar (Department of Pediatrics. University Medical Center Ulm) ;
Veys, Paul (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Fischer, Alain (Université de Paris) ;
Gennery, Andrew R. (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital)
Background: Hematopoietic stem cell transplantation (HSCT) represents a curative treatment for patients with severe combined immunodeficiency (SCID), a group of monogenic immune disorders with an otherwise fatal outcome. [...]
2022 - 10.1016/j.jaci.2021.10.017
The Journal of Allergy and Clinical Immunology, Vol. 149 Núm. 5 (may 2022) , p. 1744-1754.e8
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10 p, 723.5 KB |
Experience of the Spanish Group for Hematopoietic Transplantation (GETMON-GETH) in allogenic hematopoietic stem cell transplantation in Philadelphia acute lymphoblastic leukemia Experiencia del Grupo Español de Trasplante Hematopoyético (GETMON-GETH) en el trasplante alogénico de progenitores hematopoyéticos en leucemia aguda linfoblástica Philadelphia
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Galán Gómez, Víctor (Hospital Universitario La Paz (Madrid)) ;
de la Fuente Regaño, Lydia (Universidad Autónoma de Madrid. Facultad de Medicina) ;
Rodríguez Villa, Antonia (Hospital Universitario Reina Sofía (Còrdova, Espanya)) ;
Díaz de Heredia, Cristina (Hospital Universitari Vall d'Hebron) ;
González Vicent, Marta (Hospital Infantil Universitario Niño Jesús (Madrid)) ;
Badell Serra, Isabel (Institut d'Investigació Biomèdica Sant Pau) ;
Fernández, José María (Hospital Universitari i Politècnic La Fe (València)) ;
Pascual Martínez, Antonia Isabel (Hospital Materno Infantil Carlos Haya. Hemato-Oncología Pediátrica) ;
Pérez Hurtado, José María (Hospital Universitario Virgen del Rocío (Sevilla, Andalusia)) ;
López Duarte, Mónica (Hospital Universitario Marqués de Valdecilla (Santander, Cantabria)) ;
Maldonado Regalado, M.Soledad (Hospital Universitario Ramón y Cajal (Madrid)) ;
Pérez-Martínez, Antonio (Hospital Universitario La Paz (Madrid))
Introduction: Outcomes in patients diagnosed of acute lymphoblastic leukemia with Philadelphia chromosome (Ph-ALL) remains unfavourable compared to other subtypes of acute lymphoblastic leukemia despite improvements in drug treatments as well as advances in hematopoietic stem cell transplantation (HSCT). [...]
2022 - 10.1016/j.anpedi.2021.02.015
Anales de pediatría, Vol. 96 Núm. 4 (abril 2022) , p. 309-318
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16 p, 1.5 MB |
Risk factors and outcome of COVID-19 in patients with hematological malignancies
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Piñana, José Luis (Hospital Universitari i Politècnic La Fe (València)) ;
Martino Bofarull, Rodrigo (Institut d'Investigació Biomèdica Sant Pau) ;
García-García, Irene (Hospital Universitario Ramón y Cajal (Madrid)) ;
Parody Porras, Rocío (Institut Català d'Oncologia) ;
Morales, María Dolores (Hematology División. Hospital de Guadalajara) ;
Benzo, Gonzalo (Hospital Universitario de la Princesa (Madrid)) ;
Gómez-Catalan, Irene (Complejo Hospitalario Universitario de Albacete) ;
Coll, Rosa (Hospital Universitari de Girona Doctor Josep Trueta) ;
De La Fuente, Ignacio (Hospital Clínico Universitario de Valladolid) ;
Luna, Alejandro (Hospital Universitario Ramón y Cajal (Madrid)) ;
Merchán, Beatriz (Hematology División. Hospital de Guadalajara) ;
Chinea, Anabelle (Hospital Universitario Ramón y Cajal (Madrid)) ;
De Miguel, Dunia (Hematology División. Hospital de Guadalajara) ;
Serrano, Ana (Complejo Hospitalario Universitario de Albacete) ;
Pérez, Carmen (Hospital Clínico Universitario de Valladolid) ;
Diaz, Carola (Hospital Regional Universitario Carlos Haya (Málaga)) ;
Lopez, José Luis (Hospital Universitario Fundación Jiménez Díaz) ;
Saez, Adolfo Jesús (Hospital Universitario Ramón y Cajal (Madrid)) ;
Bailén, Rebeca (Hospital General Universitario Gregorio Marañón) ;
Zudaire, Teresa (Complejo Hospitalario de Navarra) ;
Martínez, Diana (Complejo Hospitalario Universitario de A Coruña) ;
Jurado, Manuel (Hospital Universitario Virgen de las Nieves (Granada)) ;
Calbacho, Maria (Hospital Universitario 12 de Octubre (Madrid)) ;
Vázquez, Lourdes (Hospital Universitario de Salamanca) ;
Garcia Cadenas, Irene (Institut d'Investigació Biomèdica Sant Pau) ;
Fox, Maria Laura (Vall d'Hebron Institut d'Oncologia) ;
Pimentel, Ana I. (Hospital Clínico Universitario "Lozano Blesa" de Zaragoza) ;
Bautista, Guiomar (Hospital Universitario Puerta de Hierro Majadahonda (Madrid)) ;
Nieto, Agustín (Complexo Hospitalario Universitario de Vigo) ;
Fernandez, Pascual (Hospital General Universitario de Alicante (Alacant, País Valencià)) ;
Vallejo, Juan Carlos (Hospital Universitario de Donostia (Sant Sebastià, País Basc)) ;
Solano, Carlos (Hospital Clínic Universitari (València)) ;
Valero, Marta (Hospital Arnau de Vilanova (Lleida, Catalunya)) ;
Espigado, Ildefonso (Hospital Universitario Virgen del Rocío (Sevilla, Andalusia)) ;
Saldaña, Raquel (Hospital Universitario de Jerez (Jerez de la Frontera)) ;
Sisinni, Luisa (Hospital Universitario La Paz (Madrid)) ;
Ribera, Jose-Maria (Institut Germans Trias i Pujol. Institut de Recerca contra la Leucèmia Josep Carreras) ;
Jiménez, María José (Institut Germans Trias i Pujol. Institut de Recerca contra la Leucèmia Josep Carreras) ;
Trabazo del Castillo, María (Institut d'Investigació Biomèdica Sant Pau) ;
González Vicent, Marta (Hospital Infantil Universitario Niño Jesús (Madrid)) ;
Fernández, Noemí (Hospital Universitario Marqués de Valdecilla (Santander, Cantabria)) ;
Talarn, Carme (Hospital Universitari Joan XXIII de Tarragona) ;
Montoya, Maria Carmen (Complejo Hospitalario Universitario de Albacete) ;
Cedillo, Angel (Hematopoietic Stem Cell Transplantation and Cell Therapy Group (GETH)) ;
Sureda, Anna (Institut Català d'Oncologia) ;
Universitat Autònoma de Barcelona
Background: Prognostic factors of poor outcome in patients with hematological malignancies and COVID-19 are poorly defined. Patients and methods: This was a Spanish transplant group and cell therapy (GETH) multicenter retrospective observational study, which included a large cohort of blood cancer patients with laboratory-confirmed SARS-CoV-2 infection through PCR assays from March 1st 2020 to May 15th 2020. [...]
2020 - 10.1186/s40164-020-00177-z
Experimental Hematology & Oncology, Vol. 9 Núm. 1 (25 2020) , p. 21
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17 p, 1.1 MB |
Recommendations for screening, monitoring, prevention, and prophylaxis of infections in adult and pediatric patients receiving CAR T-cell therapy : a position paper
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Los-Arcos, Ibai (Hospital Universitari Vall d'Hebron) ;
Iacoboni, Gloria (Vall d'Hebron Institut d'Oncologia) ;
Aguilar-Guisado, Manuela (Hospital Universitario Virgen del Rocío (Sevilla, Andalusia)) ;
Alsina Manrique, Laia (Hospital Sant Joan de Déu (Manresa)) ;
Díaz de Heredia, Cristina (Hospital Universitari Vall d'Hebron. Institut de Recerca) ;
Fortuny Guasch, Claudia (Hospital Sant Joan de Déu (Manresa)) ;
Garcia Cadenas, Irene (Institut d'Investigació Biomèdica Sant Pau) ;
Garcia-Vidal, Carolina (Institut d'Investigacions Biomèdiques August Pi i Sunyer) ;
González Vicent, Marta (Hospital Infantil Universitario Niño Jesús (Madrid)) ;
Hernani, Rafael (Hospital Clínic Universitari (València)) ;
Kwon, Mi (Hospital General Universitario Gregorio Marañón) ;
Machado, Marina (Hospital General Universitario Gregorio Marañón) ;
Martínez Gómez, Xavier (Hospital Universitari Vall d'Hebron) ;
Ortiz-Maldonado, Valentín (Institut d'Investigacions Biomèdiques August Pi i Sunyer) ;
Pinto Pla, Carolina (Hospital Clínic Universitari (València)) ;
Piñana, José Luis (Hospital Universitari i Politècnic La Fe (València)) ;
Pomar, Virginia (Institut d'Investigació Biomèdica Sant Pau) ;
Reguera-Ortega, Juan Luis (Hospital Universitari i Politècnic La Fe (València)) ;
Salavert, Miguel (Hospital Universitari i Politècnic La Fe (València)) ;
Soler-Palacín, Pere (Hospital Universitari Vall d'Hebron. Institut de Recerca) ;
Vázquez López, Lourdes (Hospital Universitario de Salamanca) ;
Barba, Pere (Universitat Autònoma de Barcelona. Departament de Medicina) ;
Ruiz Camps, Isabel (Universitat Autònoma de Barcelona. Departament de Medicina)
Chimeric antigen receptor (CAR) T-cell therapy is one of the most promising emerging treatments for B-cell malignancies. Recently, two CAR T-cell products (axicabtagene ciloleucel and tisagenlecleucel) have been approved for patients with aggressive B-cell lymphoma and acute lymphoblastic leukemia; many other CAR-T constructs are in research for both hematological and non-hematological diseases. [...]
2020 - 10.1007/s15010-020-01521-5
Infection, september 2020, p. 1-17
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