UAB Digital Repository of Documents 3 records found  Search took 0.00 seconds. 
1.
12 p, 2.8 MB Efficacy of adeno-associated virus gene therapy in a MNGIE murine model enhanced by chronic exposure to nucleosides / Vila-Julià, Ferran (Hospital Universitari Vall d'Hebron. Institut de Recerca) ; Cabrera-Pérez, Raquel (Hospital Universitari Vall d'Hebron. Institut de Recerca) ; Cámara, Yolanda (Hospital Universitari Vall d'Hebron. Institut de Recerca) ; Molina-Berenguer, Miguel (Hospital Universitari Vall d'Hebron. Institut de Recerca) ; Lope-Piedrafita, Silvia (Universitat Autònoma de Barcelona. Servei de Ressonància Magnètica Nuclear) ; Hirano, Michio (Department of Neurology, H. Houston Merritt Neuromuscular Research Center, Columbia University Irving Medical Center) ; Mingozzi, Federico (Spark Therapeutics) ; Torres-Torronteras, Javier (Hospital Universitari Vall d'Hebron. Institut de Recerca) ; Martí Seves, Ramon (Hospital Universitari Vall d'Hebron. Institut de Recerca)
Preclinical studies have shown that gene therapy is a feasible approach to treat mitochondrial neurogastrointestinal encephalomyopathy (MNGIE). However, the genetic murine model of the disease (Tymp/Upp1 double knockout, dKO) has a limited functional phenotype beyond the metabolic imbalances, and so the studies showing efficacy of gene therapy have relied almost exclusively on demonstrating correction of the biochemical phenotype. [...]
2020 - 10.1016/j.ebiom.2020.103133
EBioMedicine, Vol. 62 (november 2020)  
2.
95 p, 4.7 MB Fast and low-cost microbial toxicity bioassays based on electrochromic electron acceptors / Pujol Vila, Ferran ; Mas Gordi, Jordi, dir. (Universitat Autònoma de Barcelona. Departament de Genètica i de Microbiologia) ; Muñoz Berbel, Xavier, dir. ; Universitat Autònoma de Barcelona. Departament de Genètica i de Microbiologia
This thesis proposes the use of compounds that change their colour when reduced by living cells, i. e. electrochromic electron acceptors, in the development of fast and low-cost microbial toxicity bioassays suitable for in situ analysis. [...]
[Barcelona] : Universitat Autònoma de Barcelona, 2017.  
3.
1 p, 354.8 KB Design of a recombinant tissue plasminogen activator production plant / Sánchez, Carla ; Solà i Ferrando, Carles, 1945-, dir. (Universitat Autònoma de Barcelona. Departament d'Enginyeria Química, Biològica i Ambiental) ; Roca, Ramon ; Vila, Ferran ; Universitat Autònoma de Barcelona. Facultat de Biociències
2013
Grau en Biotecnologia [815]
3 documents

See also: similar author names
1 Vila, Fortià
1 Vila, Francesc
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