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10 p, 813.6 KB Rimeporide as a first- in-class NHE-1 inhibitor : Results of a phase Ib trial in young patients with Duchenne Muscular Dystrophy / Previtali, Stefano C. (IRCCS San Raffaele Scientific Institute (Milà, Itàlia)) ; Gidaro, Teresa (Hopital Trousseau) ; Diaz-Manera, Jordi (Institut d'Investigació Biomèdica Sant Pau) ; Zambon, Alberto (IRCCS San Raffaele Scientific Institute (Milà, Itàlia)) ; Carnesecchi, Stephanie (Geneva University (UNIGE)) ; Roux-Lombard, Pascale (Geneva University Hospitals) ; Spitali, Pietro (Leiden University Medical Center) ; Signorelli, Mirko (Leiden University Medical Center) ; Szigyarto, Cristina Al-Khalili (Kungl. Tekniska högskolan (Estocolm (Suècia)) ; Johansson, Camilla (Science for Life Laboratory) ; Gray, Julian (EspeRare) ; Labolle, Delphine (EspeRare) ; Porte Thomé, Florence (EspeRare) ; Pitchforth, Jacqueline (UCL Great Ormond Street Institute of Child Health & Great Ormond Street Hospital Dubowitz Neuromuscular Centre) ; Domingos, Joana (UCL Great Ormond Street Institute of Child Health & Great Ormond Street Hospital Dubowitz Neuromuscular Centre) ; Muntoni, Francesco (University College London) ; Universitat Autònoma de Barcelona
Rimeporide, a first-in-class sodium/proton exchanger Type 1 inhibitor (NHE-1 inhibitor) is repositioned by EspeRare for patients with Duchenne Muscular Dystrophy (DMD). Historically, NHE-1 inhibitors were developed for cardiac therapeutic interventions. [...]
2020 - 10.1016/j.phrs.2020.104999
Pharmacological Research, Vol. 159 (september 2020) , p. 104999  

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1 Gidaro, Teresa
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