Long-term outcomes with agalsidase alfa enzyme replacement therapy : analysis using deconstructed composite events
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Beck, Michael (University Medical Center, Mainz, Germany)
;
Hughes, Derralynn A (University College London) ;
Kampmann, Christoph (University Medical Center, Mainz, Germany) ;
Pintos-Morell, Guillem (Institut Germans Trias i Pujol. Hospital Universitari Germans Trias i Pujol) ;
Ramaswami, Uma (University College London) ;
West, Michael L. (Dalhousie University, Halifax, Canada) ;
Giugliani, Roberto (Universidade Federal do Rio Grande do Sul, Brazil) ;
Universitat Autònoma de Barcelona