Cardio-renal outcomes with long-term agalsidase alfa enzyme replacement therapy : A 10-year fabry outcome survey (FOS) analysis
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Ramaswami, Uma (Royal Free London NHS Foundation Trust. Lysosomal Disorders Unit. Institute of Immunity and Transplantation)
;
Beck, Michael (Centre for Paediatric and Adolescent Medicine. University Medical Centre. University of Mainz) ;
Hughes, D. (Royal Free London NHS Foundation Trust. Lysosomal Disorders Unit. Institute of Immunity and Transplantation) ;
Kampmann, C. (Centre for Paediatric and Adolescent Medicine. University Medical Centre. University of Mainz) ;
Botha, J. (Department of Biostatistics and Programming. Takeda) ;
Pintos-Morell, Guillem (Institut Germans Trias i Pujol. Hospital Universitari Germans Trias i Pujol) ;
West, M. L. (Department of Medicine. Dalhousie University) ;
Niu, D. M. (Department of Paediatrics. Taipei Veterans General Hospital) ;
Nicholls, K. (Royal Melbourne Hospital (Melbourne, Austràlia)) ;
Giugliani, R. (Medical Genetics Service HCPA. Department of Genetics. UFRGS. INAGEMP) ;
Universitat Autònoma de Barcelona