Access to medicines for rare diseases : beating the drum for primary ciliary dyskinesia
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Crowley, Suzanne (Oslo University Hospital (Oslo, Noruega))
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Azevedo, Ines (Universidade do Porto) ;
Boon, Mieke (University Hospitals Gasthuisberg (Leuven, Bélgica)) ;
Bush, Andrew (Royal Brompton Hospital (Londres)) ;
Eber, Ernst (Medical University of Graz) ;
Haarman, Eric (Amsterdam UMC. University Medical Center) ;
Karadag, Bulent (Marmara University) ;
Kötz, Karsten (Sahlgrenska University Hospital (Suècia)) ;
Leigh, Margaret (University of North Carolina at Chapel Hill) ;
Moreno Galdó, Antonio (Universitat Autònoma de Barcelona. Departament de Pediatria, Obstetrícia i Ginecologia i Medicina Preventiva i Salut Pública) ;
Mussaffi, Huda (Tel Aviv University) ;
Nielsen, Kim G. ;
Omran, Heymut (University Hospital Muenster (Alemanya)) ;
Papon, Jean-François (Hôpital Kremlin-Bicetre) ;
Pohunek, Petr (Charles University. Faculty of Medicine in Hradec Králové) ;
Priftis, Kostas (University General Hospital Attikon (Haidari, Grècia)) ;
Rindlisbacher, Bernhard (Patient Association Kartagener Syndrom und Primäre Ciliäre Dyskinesie e.V., Steffisburg, Switzerland) ;
Santamaria, Francesca (Federico II University) ;
Valiulis, Arunas (European Academy of Paediatrics (Bélgica)) ;
Witt, Michal (Institute of Human Genetics Polish Academy of Sciences(Polònia)) ;
Yiallouros, Panayiotis (University of Cyprus) ;
Zivkovic, Zorica (Novi Sad (Sèrbia)) ;
Kuehni, Claudia E. (University Children's Hospital Bern (Suïssa)) ;
Lucas, Jane S. (University Hospital Southampton NHS Foundation Trust (Regne Unit))