The Pyruvate Kinase Deficiency Global Longitudinal (Peak) Registry : rationale and study design
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Grace, Rachael F. (Dana-Farber/Boston Children's Cancer and Blood Disorders Center)
;
Van Beers, Eduard J. (University of Utrecht) ;
Vives Corrons, Joan Lluís (Institut Germans Trias i Pujol. Institut de Recerca contra la Leucèmia Josep Carreras) ;
Glader, Bertil (Stanford University School of Medicine) ;
Glenthøj, Andreas (Copenhagen University Hospital - Rigshospitalet) ;
Kanno, Hitoshi (Department of Transfusion Medicine and Cell Processing. Tokyo Women's Medical University) ;
Kuo, Kevin H M (University of Toronto) ;
Lander, Carl (Hammersmith Hospital (Londres)) ;
Pospíšilová, Dagmar (Department of Pediatrics. Palacky University and University Hospital) ;
Viprakasit, Vip (Mahidol University) ;
Li, Junlong (Agios Pharmaceuticals) ;
Yan, Yan (Agios Pharmaceuticals (Estats Units d'Amèrica)) ;
Boscoe, Audra N. (Agios Pharmaceuticals (Estats Units d'Amèrica)) ;
Bianchi, P. (Fondazione Irccs Ca' Granda Ospedale Maggiore Policlinico (Itàlia))