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19 p, 3.2 MB |
Hematopoietic cell transplantation in severe combined immunodeficiency : The SCETIDE 2006-2014 European cohort
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Lankester, Arjan C. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Neven, Benedicte (Institut Imagine. INSERM UMR1163. Laboratory of Immunogenetics of Pediatric Autoimmune Diseases) ;
Mahlaoui, Nizar (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
von Asmuth, Erik G.J. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Courteille, Virginie (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Alligon, Mikael (French National Reference Center for Primary Immunodeficiencies (CEREDIH) and European Registry for Stem Cell Transplantation for Primary Immunodeficiencies (SCETIDE). Hôpital Universitaire Necker-Enfants malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Albert, Michael H. (Dr von Haunersches University Children's Hospital) ;
Badell Serra, Isabel (Institut d'Investigació Biomèdica Sant Pau) ;
Bader, Peter (Department for Children and Adolescents Medicine. Division for Stem Cell Transplantation and Immunology. University Hospital Frankfurt) ;
Balashov, Dmitry (Department for Hematopoietic Stem Cell Transplantation. Dmitriy Rogachev National Center for Pediatric Hematology. Oncology and Immunology) ;
Beier, Rita (Klinik für Pädiatrische Hämatologie und Onkologie. Hannover Medical School) ;
Bertrand, Yves (Institut d'Hématologie et d'Oncologie Pédiatrique. Hospices Civils de Lyon and Université Claude Bernard Lyon 1) ;
Blanche, Stephane (Unité d'Immuno-hematologie et Rhumatologie Pédiatrique. Hôpital Universitaire Necker-Enfants Malades. Assistance Publique-Hôpitaux de Paris (AP-HP)) ;
Bordon, Victoria (Department of Pediatric Hemato-oncology and Stem Cell Transplant. Ghent University Hospital) ;
Bredius, Robert G. (Pediatric Stem Cell Transplantation Program and Laboratory for Pediatric Immunology. Willem-Alexander Children's Hospital. Leiden University Medical Center) ;
Cant, Andrew (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital) ;
Cavazzana, Marina (Laboratory of Genomic Dynamics in the Immune System. Institut Imagine. INSERM UMR1163) ;
Díaz de Heredia, Cristina (Vall d'Hebron Institut d'Oncologia) ;
Dogu, Figen (Department of PIA and the BMT Unit. Ankara University) ;
Ehlert, Karoline (Department of Pediatric Hematology and Oncology. University of Greifswald) ;
Entz-Werle, Natacha (Pediatric Onco-hematology Department-Pediatrics III. University Hospital of Strasbourg) ;
Fasth, Anders (Department of Pediatrics. Institute of Clinical Sciences. University of Gothenburg) ;
Ferrua, Francesca (Pediatric Immunohematology and Bone Marrow Transplantation Unit and the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget). IRCCS San Raffaele Scientific Institute) ;
Ferster, Alina (Department of Hemato-oncology. Hôpital Universitaire des Enfants Reine Fabiola) ;
Formankova, Renata (Department of Pediatric Hematology and Oncology. Teaching Hospital Motol. 2nd Medical School. Charles University Motol) ;
Friedrich, Wilhelm (Department of Pediatrics. University Medical Center Ulm) ;
Gonzalez-Vicent, Marta (Hospital Infantil Universitario Niño Jesús (Madrid)) ;
Gozdzik, Jolanta (Department of Clinical Immunology and Transplantation. Jagiellonian University Medical College) ;
Güngör, Tayfun (Department of Hematology. Oncology. Immunology. Gene Therapy and Stem Cell Transplantation. and Children's Research Center (CRC). University Children's Hospital) ;
Hoenig, Manfred (Department of Pediatrics. University Medical Center Ulm) ;
Ikinciogullari, Aydan (Department of PIA and the BMT Unit. Ankara University) ;
Kalwak, Krzysztof (Department of Pediatric Hematology. Oncology. and BMT. Wroclaw Medical University) ;
Kansoy, Savas (Department of Pediatric Hematology and Oncology. Ege University Hospital) ;
Kupesiz, Alphan (Department of Pediatrics. Hematology. and Oncology. Akdeniz University School of Medicine) ;
Lanfranchi, Arnalda (Diagnostic Department. Stem Cell Laboratory. Section of Hematology and Blood Coagulation. Clinical Chemistry Laboratory. ASST Spedali Civili) ;
Lindemans, Caroline A. (Department of Pediatrics. University Medical Center Utrecht. University of Utrecht) ;
Meisel, Roland (Department of Pediatric Oncology. Hematology. and Clinical Immunology. Medical Faculty. Division of Pediatric Stem Cell Therapy. Heinrich-Heine-University) ;
Michel, Gerard (Service d'Hématologie Immunologie Oncologie Pédiatrique. CHU La Timone) ;
Miranda, Nuno A. A. (BMT Unit. Instituto Português de Oncologia de Lisboa) ;
Moraleda, Jose (Instituto Murciano de Investigación Biosanitaria) ;
Moshous, Despina (Laboratory of Genomic Dynamics in the Immune System. Institut Imagine. INSERM UMR1163) ;
Pichler, Herbert (Department of Stem Cell Transplantation. Children's Cancer Institute. St Anna Hospital) ;
Rao, Kanchan (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Sedlacek, Petr (Department of Pediatric Hematology and Oncology. Teaching Hospital Motol. 2nd Medical School. Charles University Motol) ;
Slatter, Mary (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital) ;
Soncini, Elena (Pediatric Oncohaematology and BMT Unit. Children's Hospital Brescia) ;
Speckmann, Carsten (Department of Pediatric Hematology and Oncology. Center for Pediatrics and Adolescent Medicine. Institute for Immunodeficiency. Center for Chronic Immunodeficiency (CCI). Faculty of Medicine. Medical Center. University of Freiburg) ;
Sundin, Mikael (Section of Pediatric Hematology. Immunology. and HCT. Astrid Lindgren Children's Hospital. Karolinska University Hospital. and Division of Pediatrics. CLINTEC. Karolinska Institutet) ;
Toren, Amos (Paediatric Hemato-oncology and BMT. Sheba Medical Center) ;
Vettenranta, Kim (University of Helsinki and Children's Hospital. University of Helsinki) ;
Worth, Austen (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Yeşilipek, Mehmet A. (Pediatric Hematology. Oncology. and Pediatric Stem Cell Transplantation Unit. Medicalpark Antalya & Göztepe Hospitals) ;
Zecca, Marco (Pediatric Hematology/Oncology. Fondazione IRCCS Policlinico San Matteo) ;
Porta, Fulvio (Pediatric Oncohaematology and BMT Unit. Children's Hospital Brescia) ;
Schulz, Ansgar (Department of Pediatrics. University Medical Center Ulm) ;
Veys, Paul (Great Ormond Street (GOS) Hospital for Children NHS Foundation Trust and University College London GOS Institute of Child Health) ;
Fischer, Alain (Université de Paris) ;
Gennery, Andrew R. (Translational and Clinical Research Institute. Newcastle University. and the Paediatric Haematopoietic Stem Cell Transplant Unit. Great North Children's Hospital)
Background: Hematopoietic stem cell transplantation (HSCT) represents a curative treatment for patients with severe combined immunodeficiency (SCID), a group of monogenic immune disorders with an otherwise fatal outcome. [...]
2022 - 10.1016/j.jaci.2021.10.017
The Journal of Allergy and Clinical Immunology, Vol. 149 Núm. 5 (may 2022) , p. 1744-1754.e8
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11 p, 340.8 KB |
Outcomes of subsequent neoplasms after umbilical cord blood transplantation in Europe
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Rafii, Hanadi (Centre Scientifique de Monaco) ;
Ruggeri, Annalisa (IRCCS San Raffaele Scientific Institute (Milan, Itàlia)) ;
Kenzey, Chantal (Centre Scientifique de Monaco) ;
Sanz, Jaime (Hospital Universitari i Politècnic La Fe (València)) ;
Peffault De La Tour, Régis (Assistance Publique-Hôpitaux de Paris) ;
Esquirol, Albert (Hospital de la Santa Creu i Sant Pau (Barcelona, Catalunya)) ;
Michel, Gérard (Hopital pédiatrique de la Timone (Marseille, França)) ;
Chevallier, Patrice (Hospital Hotel Dieu (Nantes, França)) ;
Rubio, Marie-Thérèse (CHRU Nancy (Nancy, França)) ;
Cornelissen, Jan J. (Erasmus MC-Daniel den Hoed Cancer Centre) ;
Michallet, Mauricette (Centre Leon Berard) ;
Volt, Fernanda (Monacord, Centre Scientifique de Monaco) ;
Rivera-Franco, Monica M. (Centre Scientifique de Monaco) ;
Scigliuolo, Graziana Maria (Centre Scientifique de Monaco) ;
Cappelli, Barbara (Centre Scientifique de Monaco) ;
Rocha, Vanderson (São Paulo Medical School) ;
Gluckman, Eliane (Centre Scientifique de Monaco) ;
Universitat Autònoma de Barcelona
Subsequent neoplasms (SNs) compromise long-term survivors after hematopoietic cell transplantation. We performed a retrospective analysis of SNs in 10 358 recipients of umbilical cord blood transplantation (UCBT) from 1988 to 2018. [...]
2022 - 10.1182/bloodadvances.2022007941
Blood advances, Vol. 7 (november 2022) , p. 1976-1986
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