Elosulfase alfa for mucopolysaccharidosis type IVA : Real-world experience in 7 patients from the Spanish Morquio-A early access program - Pintos-Morell, Guillem (Institut Germans Trias i Pujol. Hospital Universitari Germans Trias i Pujol) ; Blasco Alonso, Javier (Hospital Regional Universitario de Málaga) ; Couce, Maria Luz (Hospital Clínico Universitario (Santiago de Compostela, Galícia)) ; González Gutiérrez-Solana, Luis (Hospital Infantil Universitario Niño Jesús (Madrid)) ; Guillén-Navarro, Encarnación (IMIB - Arrixaca, Murcia) ; O'Callaghan, Maria del Mar (Hospital Sant Joan de Déu (Barcelona, Catalunya)) ; Del Toro, Mireia (Hospital Universitari Vall d'Hebron) ; Universitat Autònoma de Barcelona
 
Comments (0) | Reviews (0)
Start a discussion about any aspect of this document.

 Subscribe to this discussion. You will then receive all new comments by email.

Add comment


Once logged in, authorized users can also attach files.
Note: you have not defined your nickname.
N/D will be displayed as the author of this comment.
          You can use some HTML tags: <a href>, <strong>, <blockquote>, <br />, <p>, <em>, <ul>, <li>, <b>, <i>