Rimeporide as a first- in-class NHE-1 inhibitor : Results of a phase Ib trial in young patients with Duchenne Muscular Dystrophy
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Previtali, Stefano C. (IRCCS San Raffaele Scientific Institute (Milà, Itàlia))
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Gidaro, Teresa (Hopital Trousseau) ;
Diaz-Manera, Jordi (Institut d'Investigació Biomèdica Sant Pau) ;
Zambon, Alberto (IRCCS San Raffaele Scientific Institute (Milà, Itàlia)) ;
Carnesecchi, Stephanie (Geneva University (UNIGE)) ;
Roux-Lombard, Pascale (Geneva University Hospitals) ;
Spitali, Pietro (Leiden University Medical Center) ;
Signorelli, Mirko (Leiden University Medical Center) ;
Szigyarto, Cristina Al-Khalili (Kungl. Tekniska högskolan (Estocolm (Suècia)) ;
Johansson, Camilla (Science for Life Laboratory) ;
Gray, Julian (EspeRare) ;
Labolle, Delphine (EspeRare) ;
Porte Thomé, Florence (EspeRare) ;
Pitchforth, Jacqueline (UCL Great Ormond Street Institute of Child Health & Great Ormond Street Hospital Dubowitz Neuromuscular Centre) ;
Domingos, Joana (UCL Great Ormond Street Institute of Child Health & Great Ormond Street Hospital Dubowitz Neuromuscular Centre) ;
Muntoni, Francesco (University College London) ;
Universitat Autònoma de Barcelona