Consensus recommendations for the treatment and management of patients with Fabry disease on migalastat : a modified Delphi study - Bichet, Daniel G. (University of Montréal, Canada) ; Hopkin, Robert J. (University of Cincinnati College of Medicine, United States) ; Aguiar, Patrício (Lisbon University) ; Allam, Sridhar R. (Texas Christian University, Fort Worth, United States) ; Chien, Yin-Hsiu (National Taiwan University College of Medicine, Taipei, Taiwan) ; Giugliani, Roberto (Postgraduate Program in Genetics and Molecular Biology (PPGBM) at Federal University of Rio Grande do Sul (UFRGS), Porto Alegre, Brazil) ; Kallish, Staci (University of Pennsylvania, Philadelphia, United States) ; Kineen, Sabina (Patient Advocate, United States) ; Lidove, Olivier (French Network of Inherited Metabolic Disorders (G2m), France) ; Niu, Dau-Ming (National Yang Ming Chiao Tung University, Taipei, Taiwan) ; Olivotto, Iacopo (Meyer University Children's Hospital, Florence, Italy) ; Politei, Juan (Fundacion Para el Estudio de Enfermedades Neurometabolicas (FESEN), Buenos Aires, Argentina) ; Rakoski, Paul (Patient Advocate, United States) ; Torra Balcells, Roser (Institut d'Investigació Biomèdica Sant Pau) ; Tøndel, Camilla (University of Bergen, Norway) ; Hughes, Derralynn A (University College London) ; Universitat Autònoma de Barcelona. Departament de Medicina
 
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